Journal of Genetic Syndromes & Gene Therapy
Open Access

5^th Annual Congress on Rare Diseases and Orphan Drugs

August 29-30, 2018 | Boston, USA

Keynote

• A patient at the table: How partnership with patients improves research and enhances service delivery

  Alastair Kent

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• Measuring the impact of diagnosis and treatment of rare diseases

  Alba Ancochea

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• Targeting familial Alzheimers disease

  Michael S Wolfe

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